Advancing a novel ASO therapy for Friedreich ataxia cardiomyopathy using a pre-clinical human vascularised cardiac organoid model
Author:
Jarmon G. Lees,Li Li,Haoxiang Zhang,Anne M. Kong,Andrew Treller,Geraldine M. Mitchell,Mirella Dottori,Alice Pebay,Stephen Wilcox,Mark Chong,Roger Peverill,Martin Delatyki,Jeffrey M. Pullin,Davis McCarthy,Jill S. Napierala,Marek Napierala et al.
Publication:
Journal of Molecular and Cellular Cardiology Plus