RNA trans-splicing to rescue β-catenin: A novel approach for treating CTNNB1-Haploinsufficiency disorder
Author:
Matea Maruna,Petra Sušjan-Leite,Maja Meško,Špela Miroševič,Roman Jerala
Publication:
Molecular Therapy - Nucleic Acids
© 2025 The Authors. Published by Elsevier Inc. on behalf of The American Society of Gene and Cell Therapy.