Argentine program of home infusions with enzyme replacement therapy for lysosomal diseases: Results in safety, quality of life and adherence
Author:
Guillermo Drelichman,Juan M. Politei,Nicolás Fernandez Escobar,Barbara Soberón,Nora Basack,Norberto Guelbert,Nora Watman,Norberto Antongiovanni,Fernanda Cuello,Gerardo Mogni,María Larroude,Gabriel Aguilar,Paola Reichel,Alberto Dubrovsky et al.
Publication:
Molecular Genetics and Metabolism
© 2025 Elsevier Inc. All rights are reserved, including those for text and data mining, AI training, and similar technologies.