Efficacy of sapropterin dihydrochloride (tetrahydrobiopterin, 6R-BH4) for reduction of phenylalanine concentration in patients with phenylketonuria: a phase III randomised placebo-controlled study
Author:
Harvey L Levy,Andrzej Milanowski,Anupam Chakrapani,Maureen Cleary,Philip Lee,Friedrich K Trefz,Chester B Whitley,François Feillet,Annette S Feigenbaum,Judith D Bebchuk,Heidi Christ-Schmidt,Alex Dorenbaum
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