Comparative evaluation of liver-directed knockin strategies with viral and nonviral vectors in mouse inherited disease models
Author:
Xiu Jin,Xiaoyi Wu,Junwei Song,Mei Luo,Qin Ye,Chengda Ren,Li Song,Manjun Li,Ming Hu,Yifang An,Jing Su,Jiamei Fu,Qiuxia Xu,Min Luo,Fanfei Liu,Man Liu,Qiqi Li,Shaohua Yao,Lu Chen,Yang Yang
Publication:
Molecular Therapy
© 2025 The Author(s). Published by Elsevier Inc. on behalf of The American Society of Gene and Cell Therapy.