Long-term impact of early initiation of enzyme replacement therapy in 34 MPS VI patients: A resurvey study
Author:
Dafne D.G. Horovitz,Emília K.E.A. Leão,Erlane M. Ribeiro,Ana M. Martins,Anneliese L. Barth,João I.C.F. Neri,Marcelo Kerstenetzky,Ana C.M. Siqueira,Bethania F.R. Ribeiro,Chong A. Kim,Francisca C. Santos,José F.S. Franco,Leniza C.L. Lichtvan et al.
Publication:
Molecular Genetics and Metabolism
© 2021 The Authors. Published by Elsevier Inc.