Single and Dual Vector Gene Therapy with AAV9-PHP.B Rescues Hearing in Tmc1 Mutant Mice
Author:
Jason Wu,Paola Solanes,Carl Nist-Lund,Sofia Spataro,Olga Shubina-Oleinik,Irina Marcovich,Hannah Goldberg,Bernard L. Schneider,Jeffrey R. Holt
Publication:
Molecular Therapy