Toileting Abilities Survey as a surrogate outcome measure for cognitive function: Findings from neuronopathic mucopolysaccharidosis II patients treated with idursulfase and intrathecal idursulfase
Author:
Melissa J. Hogan,Kim Stephens,Erin Smith,Elizabeth R. Jalazo,Christian J. Hendriksz,Lloyd J. Edwards,Kendra J. Bjoraker
Publication:
Molecular Genetics and Metabolism Reports
© 2020 Published by Elsevier Inc.